A Prescription Drug User Fee Act target date of September 22, 2025 has been set for the application. The Food and Drug Administration (FDA) has accepted for Priority Review the Biologics License ...

Discover how a 10-year-old boy with spinal muscular atrophy finds freedom and strength through swimming, inspiring others to defy physical limits. Read more at straitstimes.com. Read more at ...

I feel like my whole life has done a 360,” says Jesy Nelson in the final five minutes of Jesy Nelson: Life After Little Mix (Prime Video), the six-part documentary charting her life since leaving ...

Jesy Nelson broke down in tears after her campaign for more health checks on babies reached 100,000 signatures - meaning it ...

Young internet sensation Neilah, living with spinal muscular atrophy, has passed away. Her mother, Ruth Wambui, shares their ...

People with spinal muscle atrophy (SMA), an inherited neuromuscular disease, usually experience muscle weakness that impacts movement. New research suggests that electrical spinal cord stimulation ...

Infantile spinal muscular atrophy (SMA) is a neuromuscular disorder that affects the nerve cells in the spinal cord. It causes muscles to weaken and limits muscle movement. SMA is a rare condition.

Editor’s note: This is an automatically generated transcript. Please notify editor@healio.com if there are concerns regarding accuracy of the transcription. So most recently, there has been the ...

A positive newborn screening for spinal muscular atrophy (SMA) is currently considered a medical emergency. Without early treatment, severe disability or death in infancy are likely. However, research ...

Forbes contributors publish independent expert analyses and insights. Spinal muscular atrophy affects the nerves that control muscle movement, leading to progressive weakening. As a result, infants ...

SMA is a genetic condition that impacts motor neurons, leading to muscle weakness that affects essential functions like breathing and movement. Treatments like Spinraza and Zolgensma can help manage ...

As with any chronic disease, but especially with one that limits the patient’s mobility or ability to breathe, a heavy burden falls on the caregiver, be it a healthcare professional, close friend, or ...